Gene therapy needs
a paradigm shift.
The promise of gene therapy to cure diseases is falling short due to significant delivery, efficacy, and safety limitations.
Existing Nonviral Delivery Challenges
- Low Efficiency
- Temporary Expression
- Material-related Toxicities
- Poor Targeted Delivery
Viral Delivery
Challenges
- Immunogenicity
- Complex and Costly
- Tissue Biodistribution
- Payload Limitations